Press Releases

News Release – Sep 15, 2025
AMO Pharma Reports Long-Term Safety Data from REACHCDM-X Study of AMO-02 in Treatment of Congenital Myotonic Dystrophy Type 1


News Release – Sep 8, 2025
AMO Pharma Enters into License Agreement with Population Health Research Institute (PHRI) and Venca Research Inc. to Advance Largest-Ever Study in Treatment of Arrhythmogenic Right Ventricular Cardiomyopathy (ARVC)


News Release – May 2, 2024
AMO Pharma Completes Meeting with U.S. FDA and Outlines Plans to Advance Clinical Development of AMO-02 (tideglusib) in Treatment of Myotonic Dystrophy


News Release – Feb 15, 2024
AMO Pharma Announces Collaboration with Population Health Research Institute to Advance Proof of Concept Clinical Trial to Assess Efficacy of Tideglusib in Treatment of Arrhythmogenic Cardiomyopathy


News Release – Sep 19, 2023
AMO Pharma Announces Preclinical Data Showing AMO-02 Improves Muscle Function, Glucose Handling and CNS function in Mouse Models of Duchenne Muscular Dystrophy


News Release – Sep 6, 2023
AMO Pharma Announces Affirming Data from REACH-CDM Clinical Trial for AMO-02 in Treatment of Myotonic Dystrophy


News Release – Apr 25, 2023
AMO Pharma Announces Completion of Treatment of Last Patient in Pivotal REACH-CDM Clinical Trial in Myotonic Dystrophy


News Release – Feb 27, 2023
AMO Pharma Announces MHRA Confirmation of CDM1-RS as Approvable Primary Outcome Measure in Myotonic Dystrophy


News Release – Dec 6, 2022
AMO Pharma Announces Completion of Enrollment in REACH-CDM Study in Congenital Myotonic Dystrophy


News Release – May 10, 2022
AMO Pharma Announces Additional Private Equity Investment Following Progress in Phase 3 Study in Congenital Myotonic Dystrophy


News Release – Dec 22, 2021
AMO Pharma Announces Expansion of Pivotal REACH-CDM Study in Congenital Myotonic Dystrophy


News Release – Oct 14, 2021
Julia Jones Joins Amo Pharma as Chief Financial Officer and Board Member


News Release – Sept 30, 2021
AMO Pharma Announces First Patient Enrolled in REACH-CDM X 12-month Open-label Study


News Release – Aug 19, 2021
Accomplished Industry Executive Alan L. Rubino Named Chairman of AMO Pharma Board of Directors


News Release – Aug 17, 2021
AMO Pharma Awarded Innovation Passport for AMO-02 (Tideglusib) for Treatment of Congenital Myotonic Dystrophy Type 1


News Release – May 17, 2021
AMO Pharma Announces Activation of Additional Clinical Trial Sites for Pivotal REACH-CDM Study in Congenital Myotonic Dystrophy


News Release – March 3, 2021
AMO Pharma to Participate in Myotonic Dystrophy Foundation "Meet the DM Drug Developers" Program on March 5, 2021


News Release – December 22, 2020
AMO Pharma Announces Initiation of Pivotal REACH-CDM Clinical Trial for AMO-02 in Treatment of Congenital Myotonic Dystrophy


News Release – November 9, 2020
FDA Grants Rare Pediatric Disease Designation to AMO Pharma for AMO-02 for Treatment of Congenital Myotonic Dystrophy


News Release – February 28, 2020
AMO Pharma to Present at Cowen and Company 40th Annual Health Care Conference


News Release – January 9, 2020
AMO Pharma Announces Initiation of Planned Pivotal Clinical Trial for Myotonic Dystrophy Following $35m Fund Raise


News Release – September 16, 2019
AMO Pharma Participates in Workshop on Central Nervous System Involvement in Progression and Treatment of Myotonic Dystrophy During Myotonic Dystrophy Foundation Annual Conference


News Release – June 13, 2019
Updates on Development of AMO Pharma's AMO-02 Presented at International Myotonic Dystrophy Consortium Meeting


News Release - May 6, 2019
AMO Pharma Presents Statistical Analysis of Results of Phase 2 Study of AMO-02 in Adolescents with Autism Spectrum Disorder


News Release - April 16, 2019
AMO Pharma Announces Launch of First Clinician-Completed Rating Scale for Congenital Myotonic Dystrophy Type 1


News Release - October 29, 2018
AMO Pharma Reports Positive Data from Investigator-Led TIDE Study of AMO-02 in Autism Spectrum Disorder


News Release - October 23, 2018
AMO Therapeutics Announces Presentation of Concordant Analysis of Results of Phase 2 Study of AMO-02 in treatment of myotonic dystrophy


News Release - June 13, 2018
AMO Pharma Receives FDA Orphan Drug Designation for AMO-04 in Treatment of Rett Syndrome


News Release - May 7, 2018
AMO Pharma Announces Initiation of Clinical Trial conducted by Mount Sinai to Study AMO-01 in Treatment of Phelan-McDermid Syndrome


News Release - March 15, 2018
AMO Pharma Announces Results of Phase 2 Proof-of-Concept Study of AMO-02 in Congenital and Childhood Onset Myotonic Dystrophy Type 1


News Release - October 18, 2017
AMO Pharma Presents Positive Interim Analysis of Data from Congenital Myotonic Dystrophy Study at American Neurological Association Annual Meeting


News Release - September 25, 2017
AMO Pharma Reports Update on Positive Interim Analysis for the First Cohort of Phase IIa Congenital Myotonic Dystrophy Study


News Release - July 20, 2017
AMO Pharma Enters into Development and License Agreement with Numedicus Limited for Rett Syndrome Program


News Release - May 30, 2017
AMO Pharma Announces FDA Fast Track Designation For AMO-02 For Treatment Of Congenital Myotonic Dystrophy


News Release - March 14, 2017
AMO Pharma Enters into Collaboration Agreement with Ranedis Pharmaceuticals for Development of RND-001


News Release - February 28, 2017
AMO Pharma Joins with Leaders in Patient and Caregiver Advocacy to Commemorate Rare Disease Day


News Release - August 10, 2016
AMO Pharma Initiates Phase 2 Clinical Trial in UK for AMO-02 for Treatment of Congenital and Juvenile Onset Myotonic Dystrophy


News Release - June 7, 2016
AMO Pharma Presents Pre-clinical Data Showing AMO-01 Successfully Inhibits Activated Pathway Associated with Fragile X Syndrome


News Release - Apr 18, 2016
Joseph Horrigan Joins AMO Pharma as Chief Medical Officer


News Release - Sept 30, 2015
AMO Pharma Ltd. Closes $25M Private Equity Financing with Woodford Patient Capital Trust plc


In the Media

Drug Development & Delivery – March 2, 2021
DRUG DEVELOPMENT – Understanding & Targeting the Mechanism of Action of Developmental Disorders


Biotech 2050 Podcast – November 2020
Bringing new treatments to psychiatric orphan diseases, Ibs Mahmood, CEO, AMO Pharma


Clinical Leader – November 3, 2020
AMO Pharma Works With FDA To Advance CNS Trials


DDNews – October 2020
Q&A: Tackling developmental disorders through the ERK pathway


Drug Development & Delivery – September 2020
EXECUTIVE INTERVIEW – AMO Pharma: Identifying & Developing Cancer Pathway Therapeutic Candidates for Use in New Neurological Indications


Global Genes' RARECast – May 21, 2020
An Approach to De-Risk Rare Disease Drug Development


Biospace – May 8, 2020
AMO Drug May Restore Normal Learning Function in Some Genetic Brain Diseases


CheckRare – May 7, 2020
AMO Pharma's Pipeline: CMD, Phelan-McDermid, and Rett Syndrome


CheckRare – May 7, 2020
Congenital Myotonic Dystrophy


Muscular Dystrophy News Weekly Digest - January 22, 2020
Enrollment Starts for Phase 2/3 Trial of Oral Therapy for Congenital DM1


News Release - May 28, 2019
How Development Of A Clinical Rating Scale Provided Deeper Insights In A Rare Disease Trial


Can a Pharma Drug Improve Autism Conditions? - November 1, 2018

https://www.biospace.com/article/can-a-pharma-drug-improve-autism-conditions-

 

Tideglusib Improves Myotonic Dystrophy Type 1 Neuromuscular Symptoms - October 31, 2018

https://www.neurologylive.com/clinical-focus/tideglusib-improves-patients-myotonic-dystrophy-type-1

 

AMO Pharma Reports Positive Results from AMO-02 Trial - October 30, 2018

https://www.drugdevelopment-technology.com/news/amo-pharma-reports-positive-results-from-tide-trial/

 

Positive Data for AMO-02 in Autism Spectrum Disorder - October 30, 2018

https://www.thepharmaletter.com/article/positive-data-for-amo-02-in-autism-spectrum-disorder

 

Orphan Drug Update: Phase 2 Study Shows Promise in Congenital and Childhood Onset Myotonic Dystrophy Type 1 - October 28, 2018

https://medicalresearch.com/pediatrics/orphan-drug-update-phase-2-study-shows-promise-in-congenital-and-childhood-onset-myotonic-dystrophy-type-1/45536

 

FDA Grants Orphan Drug Designation to New Treatment for Rett Syndrome - June 15, 2018

https://www.raredr.com/news/fda-grants-orphan-drug-designation-to-new-treatment-for-rett-syndrome

 

Phelan-McDermid Syndrome Treatment Commences Clinical Trial Recruitment - May 11, 2018

http://www.raredr.com/news/phelanmcdermid-syndrome-treatment-commences-clinical-trial-recruitment

 

AMO Pharma Announces Initiation of Clinical Trial conducted by Mount Sinai to Study AMO-01 in Treatment of Phelan-McDermid Syndrome - May 8, 2018

http://www.checkorphan.org/news/amo-pharma-announces-initiation-of-clinical-trial-conducted-by-mount-sinai-to-study-amo-01-in-treatment-of-phelan-mcdermid-syndrome

 

AMO Pharma Advancing Ultra-Rare Program on Back of Phase IIb Data - April 10, 2018

http://www.bioworld.com/content/amo-pharma-advancing-ultra-rare-program-back-phase-iib-data/

 

Early Clinical Trials of AMO-02 Show Promise in Congenital and Childhood Myotonic Dystrophy Type 1 - March 23, 2018

https://medicalresearch.com/author-interviews/early-clinical-trials-of-amo-02-show-promise-in-congenital-and-childhood-myotonic-dystrophy-type-1/40741/

 

Companies pair up to take Rett Syndrome program into clinic - July 20, 2017

https://www.thepharmaletter.com/article/companies-pair-up-to-take-rett-syndrome-program-into-clinic/

 

News of Note—Trevena CMO exit; AMO deal; Kala IPO; AliveCor-Mayo pact - July 20, 2017

http://www.fiercebiotech.com/biotech/news-note-trevena-cmo-exit-amo-deal-kala-ipo-alivecor-mayo-pact

 

FDA Gives Fast Track Status to Potential Therapy for Congenital Myotonic Dystrophy - June 1, 2017

https://musculardystrophynews.com/2017/06/01/amo-02-congenital-myotonic-dystrophy-treatment-gains-fda-fast-track/

 

AMO Pharma receives FDA Fast Track Status - May 30, 2017

http://european-biotechnology.com/up-to-date/latest-news/news/amo-pharma-receives-fda-fast-track-status.html

 

FDA Fast Tracks Muscular Dystrophy Drug backed by Woodford - May 30, 2017

http://labiotech.eu/amo-pharma-amo-02-myotonic-dystrophy/

 

AMO Pharma Addresses Rare Childhood Disease - May 22, 2017

https://www.clinicalleader.com/doc/amo-pharma-addresses-rare-childhood-disease-0001

 

Ranedis and AMO Partner to Develop HDAC Inhibitor for Rare Genetic Diseases - March 14, 2017

http://www.genengnews.com/gen-news-highlights/ranedis-and-amo-partner-to-develop-hdac-inhibitor-for-rare-genetic-diseases/81254020

 

AMO Pharma and Ranedis target rare genetic diseases in RND-001 deal - March 14, 2017

https://www.thepharmaletter.com/article/amo-pharma-and-ranedis-target-rare-genetic-diseases-in-rnd-001-deal

 

Wayne-Based AMO Pharma Raises $25 Million - October 1, 2015

https://patch.com/pennsylvania/te/wayne-based-amo-pharma-raises-25-million

 

Neil Woodford's Latest €25M UK Biotech pay-out is to AMO Pharma - October 1, 2015

http://labiotech.eu/neil-woodford-amo-pharma-25m/

 

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